PTC THERAPEUTICS, INC. (NASDAQ:PTCT) Files An 8-K Other Events
Item 8.01. Other Events.

On October 5, 2018, supplemental information on the FIREFISH study that was the subject of the press release issued by PTC Therapeutics, Inc. on October 3, 2018, was presented by a principal investigator in the trial. As disclosed in the original press release, interim data showed a total of three babies sitting unassisted. On October 5, 2018, the principal investigator showed a video of an additional SMA type 1 baby sitting unassisted. The video also showed SMA type 1 babies from the FIREFISH trial demonstrating head control and rolling.

A copy of the press release issued on October 3, 2018, is attached to this Current Report on Form 8-K as Exhibit 99.1.

(d) Exhibits

PTC THERAPEUTICS, INC. Exhibit
EX-99.1 2 a2018-10x03ptct2018wmssmax.htm EXHIBIT 99.1 Exhibit Risdiplam Demonstrates Preliminary Evidence of Clinical Benefit in Type 1,…
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About PTC THERAPEUTICS, INC. (NASDAQ:PTCT)

PTC Therapeutics, Inc. is a biopharmaceutical company focused on the discovery, development and commercialization of orally administered, small molecule therapeutics that focus on post-transcriptional control processes. The Company’s lead product, Translarna (ataluren), is used for the treatment of nonsense mutation Duchenne muscular dystrophy (nmDMD) in ambulatory patients with age of over five years and older. Its programs include Translarna for nonsense mutation cystic fibrosis (nmCF), Translarna for mucopolysaccharidosis type I caused by nonsense mutation (nmMPS I), Translarna for nonsense mutation aniridia, Translarna for nonsense mutation Dravet syndrome/CDKL5, Spinal muscular atrophy (SMA) in collaboration with Spinal Muscular Atrophy Foundation (SMA Foundation) and F. Hoffman-La Roche Ltd and Hoffman- La Roche Inc. (collectively Roche), and Cancer stem cell program (PTC596). It has two compounds in clinical development within the SMA program: RG7800 and RG7916.